Tag Archives: sickle cell disease

Sanofi’s Rilzabrutinib Granted Fourth Orphan Drug Designation, Now Targeting Sickle Cell Disease

(IN BRIEF) Rilzabrutinib, an oral Bruton’s tyrosine kinase (BTK) inhibitor, has received orphan drug designation from the U.S. FDA for sickle cell disease. This marks the fourth such designation for the drug, which has already been recognized for its potential … Read the full press release

Genetic diversity: GSK and Novartis launch Project Africa GRADIENT to optimise treatment responses for malaria and tuberculosis in Africa

Project Africa GRADIENT calls on local researchers to submit proposals exploring the link between genetic diversity and response to malaria and tuberculosis drugs in African patients. Combined funding commitment of GBP 2.8 million (USD 3.6 million) over five years. Researchers … Read the full press release