rare diseases

AstraZeneca Teams Up with Cellectis to Accelerate Gene Therapy Development

(IN BRIEF) AstraZeneca has entered into a collaboration and investment agreement with biotech firm Cellectis to fast-track the development of…

6 months ago

Sanofi launches more impactful Corporate Social Responsibility (CSR) strategy

Accelerating projects on access to medicines, support for vulnerable communities, environmental conservation, and diversity and inclusion Creation of Sanofi Global Health, global…

3 years ago

Rare disease: Enhertu of AstraZeneca and Daiichi Sankyo now with Orphan Drug Designation in the US for treatment of gastric cancer

(PRESS RELEASE) CAMBRIDGE, 22-May-2020 — /EuropaWire/ — Enhertu, jointly developed by British-Swedish multinational pharmaceutical and biopharmaceutical company AstraZeneca and the…

4 years ago

Shire: U.S. FDA approval makes CINRYZE® available to help prevent angioedema attacks in children with hereditary angioedema

CINRYZE is the first and only therapy indicated in the U.S. to help prevent angioedema attacks in pediatric patients with…

6 years ago

U.S. FDA approval for Shire’s first submission for its new plasma manufacturing facility near Covington, Georgia

New facility will add 30% capacity to Shire’s internal plasma manufacturing network once fully operational Expanded capacity supports continued strong…

6 years ago

Alliance Life Sciences is a Sponsor at World Pharma Pricing and Market Access Congress 2018, Showcasing Data and Technology Solutions

World Pharma Pricing and Market Access Congress 2018 Business Design Centre, London United Kingdom SOMERSET, N.J. / LONDON, UK, 19-Mar-2018…

6 years ago

Sanofi acquires Bioverativ Inc., a biopharmaceutical company focused on therapies for hemophilia and other rare blood disorders

Expands Sanofi’s presence in specialty care and strengthens leadership in rare diseases  Adds leader in the growing hemophilia market and…

6 years ago

Shire CMO Howard Mayer, M.D.: no patient is currently being denied access to treatment with Hemlibra

DUBLIN, 16-Jan-2018 — /EuropaWire/ — At Shire, we’ve been committed to the hemophilia community and the lives of every patient afflicted…

6 years ago

Shire: EU approval of ADYNOVI is an important milestone in our continued commitment to provide new treatment options for patients with hemophilia A

Marketing Authorization will enable patient access to ADYNOVI throughout Europe ZUG, 16-Jan-2018 — /EuropaWire/ — Shire plc (LSE: SHP, NASDAQ: SHPG),…

6 years ago

200 healthcare decision-makers gather to address the looming challenges of cost, access and sustainability in the coming wave of high-value medicines

LONDON, 01-Dec-2017 — /EuropaWire/ — On December 5-6, 2017, 200 high-level experts from government, academia, biopharmaceutical developers and patient organisations…

6 years ago

EURORDIS: Rare diseases are not yet recognised as an international public health priority

BRUSSELS, 18-3-2015 — /EuropaWire/ — The 22nd meeting of the EURORDIS Round Table of Companies recently took place in Brussels…

9 years ago

EURORDIS: Participants in over 80 countries join together for better care on the Rare Disease Day 2014

Paris, France, 28-2-2014 — /EuropaWire/ — Today is our day. 28 February 2014. Rare Disease Day 2014. Let the world know! There…

10 years ago

Rare Disease Day: Novartis hosts 2nd international conference dedicated to the research of rare and orphan diseases

Company is pleased to host second international conference dedicated to the research of rare and orphan diseases Novartis is engaging…

10 years ago

EU Health Prize for Journalists seeks to reward excellence in health journalism, now open to 28 European countries

Brussels, 14-6-2013 — /europawire.eu/ — Today, the virtual doors swing open to journalists from across the EU wishing to participate in the…

11 years ago