Tag Archives: treatment

GEMINI Study Identifies Genetic Links to Multimorbidity, Offering New Pathways for Prevention and Treatment

(IN BRIEF) The GEMINI study, the largest of its kind, has revealed significant genetic overlaps in 72 long-term health conditions related to aging. Conducted by the University of Exeter Medical School and funded by the Medical Research Council and the … Read the full press release

EESC Calls for European Action Plan on Rare Diseases to Improve Diagnosis and Treatment

(IN BRIEF) The European Economic and Social Committee (EESC) has called for a comprehensive European Action Plan on Rare Diseases by 2030, urging the EU and Member States to enhance cooperation and ensure equal access to diagnosis and treatment. At … Read the full press release

EMA Approves Dupixent as First-Ever Treatment for Young Children with Eosinophilic Esophagitis in the EU

(IN BRIEF) The European Medicines Agency has approved Dupixent as the first treatment for eosinophilic esophagitis (EoE) in young children aged one to 11, marking a significant step in managing this condition in a critical developmental phase. The approval is … Read the full press release

Ultomiris Receives FDA Approval as First Long-Acting Treatment for AQP4 Ab+ NMOSD, Redefining Patient Care

(IN BRIEF) Ultomiris (ravulizumab-cwvz) has gained approval from the FDA as the inaugural long-acting C5 complement inhibitor for treating adult patients with anti-aquaporin-4 (AQP4) antibody-positive (Ab+) neuromyelitis optica spectrum disorder (NMOSD). The approval, based on the CHAMPION-NMOSD Phase III trial’s … Read the full press release

Boehringer Ingelheim and Sosei Heptares Forge Global Collaboration to Pioneer Precision Treatment for Schizophrenia

(IN BRIEF) Boehringer Ingelheim and Sosei Group Corporation (Sosei Heptares) have unveiled a global collaboration and exclusive option-to-license agreement aimed at advancing the development and commercialization of Sosei Heptares’ portfolio of first-in-class GPR52 agonists. The focus of this collaboration lies … Read the full press release

Voydeya Recommended for EU Marketing Authorization as PNH Treatment Add-On

(IN BRIEF) Voydeya (danicopan), a first-in-class oral Factor D inhibitor, has been recommended for marketing authorization in the European Union (EU) as an add-on to ravulizumab or eculizumab for adult patients with paroxysmal nocturnal haemoglobinuria (PNH) who experience residual haemolytic … Read the full press release

GSK’s Gepotidacin Shows Promise as Gonorrhoea Treatment: Positive Results from EAGLE-1 Trial

(IN BRIEF) GSK plc has announced positive headline results from the pivotal EAGLE-1 phase III trial for gepotidacin, an oral antibiotic aimed at treating uncomplicated urogenital gonorrhoea in adolescents and adults. The trial demonstrated gepotidacin’s non-inferiority compared to the current … Read the full press release

Boehringer Ingelheim’s Survodutide Shows Promising Results as Potential Best-in-Class Treatment for MASH in Phase II Trial

(IN BRIEF) Boehringer Ingelheim has reported compelling results from its Phase II trial of Survodutide, a novel glucagon/GLP-1 receptor dual agonist, indicating its potential to become a leading treatment for Metabolic Dysfunction-Associated Steatohepatitis (MASH). In the trial, up to 83.0% … Read the full press release

Acoramidis Shows Positive Results in Japanese Trial for Treating Transthyretin-Mediated Amyloid Cardiomyopathy (ATTR-CM)

(IN BRIEF) In a Phase III trial conducted in Japan, acoramidis, an investigational treatment for transthyretin-mediated amyloid cardiomyopathy (ATTR-CM), demonstrated promising high-level results consistent with the global BridgeBio Pharma, Inc. ATTRibute-CM Phase III trial. The trial in Japan aimed to … Read the full press release

GUSTO Trial Aims to Revolutionize Bladder Cancer Treatment with Genetic Tailoring

(IN BRIEF) A groundbreaking trial called GUSTO, led jointly by the University of Southampton, Sheffield Teaching Hospitals NHS Foundation Trust, and the University of Leeds, has been launched to potentially revolutionize bladder cancer treatment by matching therapies to the genetic … Read the full press release

Groundbreaking Treatment Tezepelumab Offers Hope to Severe Asthma Patients

(IN BRIEF) Researchers at the University of Leicester have developed a groundbreaking treatment for severe asthma using the monoclonal antibody tezepelumab. This monthly injection targets thymic stromal lymphopoietin (TSLP), a substance associated with inflammation in the airways of severe asthma … Read the full press release

ViiV Healthcare Receives Chinese Approval for Long-Acting HIV Treatment Vocabria and Rekambys

(IN BRIEF) ViiV Healthcare has received approval from China’s National Medical Products Administration (NMPA) for Vocabria (cabotegravir) in combination with Rekambys (rilpivirine), marking the first complete long-acting HIV-1 injectable treatment in China. This approval allows people living with HIV in … Read the full press release

GSK’s ViiV Healthcare to Share Latest Advances in HIV Treatment and Prevention at EACS 2023

(IN BRIEF) ViiV Healthcare, a global specialist HIV company, will present 23 abstracts at the 19th Annual European AIDS Conference (EACS 2023). These abstracts will cover various aspects of HIV treatment and prevention, including real-world data on long-acting and 2-drug … Read the full press release

GSK’s Jemperli Receives Positive CHMP Opinion for Frontline Treatment of Advanced Endometrial Cancer with Chemotherapy

(IN BRIEF) GSK has received a positive opinion from the Committee for Medicinal Products for Human Use (CHMP) of the European Medicines Agency (EMA) for the approval of Jemperli (dostarlimab) in combination with chemotherapy as a frontline treatment for adult … Read the full press release

Alexion to Present Data Reinforcing Effectiveness of Ultomiris and Soliris in Treating Rare Neurological Disorder at ECTRIMS-ACTRIMS Meeting

(IN BRIEF) Alexion, a subsidiary of AstraZeneca Rare Disease, is set to present new data at the 9th Joint Meeting of the European Committee for Treatment and Research in Multiple Sclerosis and Americas Committee for Treatment and Research in Multiple … Read the full press release

Roche’s OCREVUS Subcutaneous Injection Shows Promise in Phase III Study for Multiple Sclerosis Treatment

(IN BRIEF) Roche has announced positive late-breaking data from the Phase III OCARINA II study, which demonstrates the effectiveness of OCREVUS as a twice-yearly, 10-minute subcutaneous injection for patients with relapsing or primary progressive multiple sclerosis (RMS or PPMS). The … Read the full press release

Merck’s Evobrutinib Shows Long-Term Efficacy and Improved Quality of Life in Multiple Sclerosis Patients, Revealing Potential RMS Treatment Advancements

(IN BRIEF) Merck has presented new data on evobrutinib, an investigational BTK inhibitor, at the 9th Joint ECTRIMS-ACTRIMS congress. The data from an ongoing Phase II open-label extension study of evobrutinib in patients with relapsing multiple sclerosis (RMS) show sustained … Read the full press release

Sanofi’s ALTUVIIIO Granted Marketing Authorization in Japan for Hemophilia A Treatment

(IN BRIEF) The Japanese Ministry of Health, Labor, and Welfare (MHLW) has granted marketing authorization for ALTUVIIIO, a novel factor VIII replacement therapy used to control bleeding in patients with hemophilia A. ALTUVIIIO, also known as efanesoctocog alfa, stands out … Read the full press release

Internet-Delivered Cognitive Behavioral Therapy Offers Cost-Effective Alternative for Depression and Anxiety Treatment, Study Finds

(IN BRIEF) A study conducted by the University of York, in collaboration with ieso Digital Health Ltd and Dorset HealthCare University NHS Trust, has found that internet-delivered cognitive behavioral therapy (CBT) offers greater cost-effectiveness and comparable clinical effectiveness compared to … Read the full press release

Switzerland’s First Proton Radiotherapy for Oesophageal Cancer Conducted in Landmark Clinical Trial

(IN BRIEF) The Paul Scherrer Institute (PSI) has administered proton radiotherapy to a 67-year-old patient with oesophageal cancer, marking the first time this treatment has been used in Switzerland for such a case. The treatment is part of a collaborative … Read the full press release